نتایج جستجو برای: congenital myasthenic syndrome

تعداد نتایج: 719275  

Journal: :بینا 0
مصطفی سلطان سنجری soltan sanjari تهران- خیابان ستارخان- خیابان نیایش- بیمارستان حضرت رسول اکرم (ص)- مرکز تحقیقات چشم محسن همنی کشکولی bahmani kashkoli تهران- خیابان ستارخان- خیابان نیایش- بیمارستان حضرت رسول اکرم (ص)- مرکز تحقیقات چشم محمدمهدی پرورش parvaresh تهران- خیابان ستارخان- خیابان نیایش- بیمارستان حضرت رسول اکرم (ص)- مرکز تحقیقات چشم

purpose: to report two sisters with congenital myasthenic syndrome (cms) masquerading as myasthenia gravis. patients and findings: two six and seven years old sisters presented with variable strabismus, ptosis, and fatigue. all symptoms were aggravated with exercise and improved with rest. intramuscular prostigmin injection decreased their symptoms. a diagnosis of cms was made according to earl...

Journal: :Handbook of clinical neurology 1998
Daniel Hantaï Pascale Richard Jeanine Koenig Bruno Eymard

PURPOSE OF REVIEW Congenital myasthenic syndromes are a heterogeneous group of diseases caused by genetic defects affecting neuromuscular transmission. In this article, a strategy that leads to the diagnosis of congenital myasthenic syndromes is presented, and recent advances in the clinical, genetic and molecular aspects of congenital myasthenic syndrome are outlined. RECENT FINDINGS Besides...

2015
Katsiaryna Belaya Pedro M. Rodrı́guez Cruz Wei Wei Liu Susan Maxwell Simon McGowan Maria E. Farrugia Richard Petty Timothy J. Walls Maryam Sedghi Keivan Basiri Wyatt W. Yue Anna Sarkozy Marta Bertoli Matthew Pitt Robin Kennett Andrew Schaefer Kate Bushby Matt Parton Hanns Lochmüller Jacqueline Palace Francesco Muntoni David Beeson

Congenital myasthenic syndromes are inherited disorders that arise from impaired signal transmission at the neuromuscular junction. Mutations in at least 20 genes are known to lead to the onset of these conditions. Four of these, ALG2, ALG14, DPAGT1 and GFPT1, are involved in glycosylation. Here we identify a fifth glycosylation gene, GMPPB, where mutations cause congenital myasthenic syndrome....

2015
Katsiaryna Belaya Pedro M. Rodríguez Cruz Wei Wei Liu Susan Maxwell Simon McGowan Maria E. Farrugia Richard Petty Timothy J. Walls Maryam Sedghi Keivan Basiri Wyatt W. Yue Anna Sarkozy Marta Bertoli Matthew Pitt Robin Kennett Andrew Schaefer Kate Bushby Matt Parton Hanns Lochmüller Jacqueline Palace Francesco Muntoni David Beeson

Congenital myasthenic syndromes are inherited disorders that arise from impaired signal transmission at the neuromuscular junction. Mutations in at least 20 genes are known to lead to the onset of these conditions. Four of these, ALG2, ALG14, DPAGT1 and GFPT1, are involved in glycosylation. Here we identify a fifth glycosylation gene, GMPPB, where mutations cause congenital myasthenic syndrome....

2016
Emily O’Connor Ana Töpf Juliane S. Müller Daniel Cox Teresinha Evangelista Jaume Colomer Angela Abicht Jan Senderek Oswald Hasselmann Ahmet Yaramis Steven H. Laval Hanns Lochmüller

Congenital myasthenic syndromes are a group of rare and genetically heterogenous disorders resulting from defects in the structure and function of the neuromuscular junction. Patients with congenital myasthenic syndrome exhibit fatigable muscle weakness with a variety of accompanying phenotypes depending on the protein affected. A cohort of patients with a clinical diagnosis of congenital myast...

2016
Emily O’Connor Ana Töpf Juliane S. Müller Daniel Cox Teresinha Evangelista Jaume Colomer Angela Abicht Jan Senderek Oswald Hasselmann Ahmet Yaramis Steven H. Laval Hanns Lochmüller

Congenital myasthenic syndromes are a group of rare and genetically heterogenous disorders resulting from defects in the structure and function of the neuromuscular junction. Patients with congenital myasthenic syndrome exhibit fatigable muscle weakness with a variety of accompanying phenotypes depending on the protein affected. A cohort of patients with a clinical diagnosis of congenital myast...

Journal: :Pediatric Neurology Briefs 2001

Journal: :Indian pediatrics 2015
S Khadilkar A Bhutada B Nallamilli M Hegde

BACKGROUND Congenital Myasthenic Syndromes (CMS) are heterogeneous genetic diseases. CASE CHARACTERISTICS Two siblings presented with progressive limb girdle weakness without significant fluctuations or ocular muscle weakness. Repetitive nerve stimulation showed a decremental response and there was no response to pyridostigmine therapy. OUTCOME A trial of salbutamol produced a remarkable, c...

Journal: :Clinical Neurophysiology 2020

Journal: :Journal of Neurology, Neurosurgery & Psychiatry 1987

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