نتایج جستجو برای: maroteaux lamy syndrome

تعداد نتایج: 622119  

Journal: :Molecular genetics and metabolism 2015
Yew Sing Choy Kaustuv Bhattacharya Shanti Balasubramaniam Michael Fietz Antony Fu Anita Inwood Dong-Kyu Jin Ok-Hwa Kim Motomichi Kosuga Young Hee Kwun Hsiang-Yu Lin Shuan-Pei Lin Nancy J Mendelsohn Torayuki Okuyama Hasri Samion Adeline Tan Akemi Tanaka Verasak Thamkunanon Meow-Keong Thong Teck-Hock Toh Albert D Yang Jim McGill

Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrome) is caused by deficient activity of the enzyme, N-acetylgalactosamine-4-sulfatase, resulting in impaired degradation of the glycosaminoglycan dermatan sulfate. Patients experience a range of manifestations including joint contractures, short stature, dysostosis multiplex, coarse facial features, decreased pulmonary function, cardiac abno...

Journal: :Human heredity 2014
Fabiana Moura Costa-Motta Fernanda Bender Angelina Acosta Kiyoko Abé-Sandes Taísa Machado Thaís Bomfim Tatiana Boa Sorte Danniel da Silva Alan Bittles Roberto Giugliani Sandra Leistner-Segal

Mucopolysaccharidosis type VI (MPS VI - Maroteaux-Lamy syndrome) is a globally rare lysosomal storage disease caused by a deficiency of arylsulfatase B. However, in Monte Santo, a poor and isolated rural region in Northeast Brazil with large family sizes and high rates of community endogamy and parental consanguinity (α = 0.00483), 9 living and 4 now deceased individuals in 11 kindreds have bee...

Journal: :Molecular genetics and metabolism 2007
Elena Garrido Amparo Chabás Maria Josep Coll Mariana Blanco Carmen Domínguez Daniel Grinberg Lluïsa Vilageliu Bru Cormand

Maroteaux-Lamy syndrome, or mucopolysaccharidosis VI (MPS VI), is an autosomal recessive lysosomal storage disorder caused by a deficiency of N-acetylgalactosamine-4-sulfatase or arylsulfatase B (ARSB). We aimed to analyze the spectrum of mutations responsible for the disorder in Spanish and Argentinian patients, not previously studied. We identified all the ARSB mutant alleles, nine of them no...

Journal: :The Biochemical journal 1990
J A Taylor G J Gibson D A Brooks J J Hopwood

The biosynthesis and maturation of N-acetylgalactosamine-4-sulphatase (4-sulphatase) was studied in normal fibroblasts and in fibroblasts from patients with either mucopolysaccharidosis type VI (MPS VI; Maroteaux-Lamy syndrome) or multiple sulphatase deficiency (MSD). Fibroblasts were incubated in culture medium containing [3H]leucine or [35S]methionine, and radiolabelled 4-sulphatase was isola...

2016
Ali Al Kaissi Jochen Hofstaetter Gerlinde Weigel Franz Grill Rudolf Ganger Susanne Gerit Kircher

INTRODUCTION A 13-year-old child was clinically diagnosed with mucopolysaccharidosis type VI-Maroteaux-Lamy syndrome (MPS VI) at the age of 5 years, and the diagnosis was confirmed biochemically and genetically (homozygous mutation in ARSB gene). At that time, his older brother manifested with increasing severe mental retardation. His urinary glycosaminoglycan excretion in urine was elevated, b...

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