In vivo versus ex vivo CRISPR therapies for retinal dystrophy
نویسندگان
چکیده
منابع مشابه
Innovations Needed for Effective Implementation of Ex Vivo Gene Therapies
Over the past decade, therapy based on gene addition to hematopoietic stem progenitor cells (HSPCs) has achieved unprecedented curative outcomes for several genetic diseases, such as X-linked severe combined immunodeficiency (X-SCID) (1), adenosine deaminase deficiency (2), metachromatic leukodystrophy (3), hemoglobinopathies (4), and Wiskott–Aldrich syndrome (WAS) (5). Recent developments in g...
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متن کاملLinarin Inhibits the Acetylcholinesterase Activity In-vitro and Ex-vivo
Linarin is a flavone glycoside in the plants Flos chrysanthemi indici, Buddleja officinalis, Cirsium setosum, Mentha arvensis and Buddleja davidii, and has been reported to possess analgesic, antipyretic, anti-inflammatory and neuroprotective activities. In this paper, linarin was investigated for its AChE inhibitory potential both in vitro and ex vivo. Ellman’s colorimetric method was used for...
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ژورنال
عنوان ژورنال: Expert Review of Ophthalmology
سال: 2016
ISSN: 1746-9899,1746-9902
DOI: 10.1080/17469899.2016.1251316