نتایج جستجو برای: x linked recessive

تعداد نتایج: 848601  

Journal: :The Journal of clinical investigation 1992
G de Saint-Basile F Le Deist M Caniglia Y Lebranchu C Griscelli A Fischer

Seven forms of X-linked (XL) immunodeficiency have been described (XL agammaglobulinemia, XL severe combined immunodeficiency [SCID], Wiskott-Aldrich syndrome, XL chronic granulomatous disease, XL hyper-IgM syndrome with low IgG and IgA, and XL lymphoproliferative syndrome), and properdine deficiency. Although there are (some) phenotypic variants, diagnosis is relatively simple on the basis of ...

2013
Young-Mi Han Kyoung-Ah Kwon Yun-Jin Lee Sang-Ook Nam Kyung-Hee Park Shin-Yun Byun Gu-Hwan Kim Han-Wook Yoo

X-linked recessive myotubular myopathy (XLMTM) is a severe congenital muscle disorder caused by mutations in the MTM1 gene and characterized by severe hypotonia and generalized muscle weakness in affected males. It is generally a fatal disorder during the neonatal period and early infancy. The diagnosis is based on typical histopathological findings on muscle biopsy, combined with suggestive cl...

2013
Gyda Hlin Skuladottir Jack Karolina Malm-Willadsen Anja Frederiksen Dorte Glintborg Marianne Andersen

Adrenoleukodystrophy (ALD) is a rare X-linked inherited leukodystrophy with a reduced capacity for degradation of very long chain fatty acids (VLCFAs). The intracellular accumulation of VLCFA leads to demyelination in the central nervous system (CNS) and cell destruction in the adrenal glands. ALD primarily affects males; however, females may develop milder symptoms that may be difficult to rec...

Journal: :Genomics 2002
Radha Ayyagari F Yesim Demirci Jiafan Liu Eve L Bingham Heather Stringham Laura E Kakuk Michael Boehnke Michael B Gorin Julia E Richards Paul A Sieving

We mapped a new X-linked recessive atrophic macular degeneration locus to Xp21.1-p11.4 and show allelic involvement of the gene RPGR, which normally causes severe peripheral retinal degeneration leading to global blindness. Ten affected males whom we examined had primarily macular atrophy causing progressive loss of visual acuity with minimal peripheral visual impairment. One additional male sh...

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