نتایج جستجو برای: adrenoleukodystrophy

تعداد نتایج: 2020  

Journal: :Journal of Inherited Metabolic Disease 2021

Journal: :Journal of Neurology, Neurosurgery & Psychiatry 1989

Journal: :Stem Cell Research 2021

Adrenoleukodystrophy (ALD) is an X-linked genetic disorder, characterized by demyelination in the central nervous system and adrenal insufficiency. Human induced pluripotent stem cell (hiPSC) lines derived from two Japanese male patients with ALD were generated skin fibroblasts using retroviral vectors. The hiPSC showed self-renewal pluripotency, carried either a missense or nonsense mutation A...

2017
Fang Yan Wenbo Wang Hui Ying Hongyu Li Jing Chen Chao Xu

X-linked adrenoleukodystrophy (X-ALD) is the most common peroxisomal disorder. It is a heterogeneous disorder caused by mutations in the ATP-binding cassette protein subfamily D1 (ABCD1) gene, encoding the peroxisomal membrane protein ALDP, which is involved in the transmembrane transport of very long-chain fatty acids. For the first time, we report a case of olivopontocerebellar X-ALD on the C...

Journal: :The Journal of biological chemistry 2012
Merle Hillebrand Søren W Gersting Amelie S Lotz-Havla Annika Schäfer Hendrik Rosewich Oliver Valerius Ania C Muntau Jutta Gärtner

The neurodegenerative disease X-linked adrenoleukodystrophy (X-ALD) is characterized by the abnormal accumulation of very long chain fatty acids. Mutations in the gene encoding the peroxisomal ATP-binding cassette half-transporter, adrenoleukodystrophy protein (ALDP), are the primary cause of X-ALD. To gain a better understanding of ALDP dysfunction, we searched for interaction partners of ALDP...

Journal: :Neurobiology of disease 2007
Romana Höftberger Markus Kunze Isabelle Weinhofer Fahmy Aboul-Enein Till Voigtländer Iris Oezen Gabriele Amann Hanno Bernheimer Herbert Budka Johannes Berger

Defects of adrenoleukodystrophy protein (ALDP) lead to X-linked adrenoleukodystrophy (X-ALD), a disorder mainly affecting the nervous system white matter and the adrenal cortex. In the present study, we examine the expression of ALDP in various human tissues and cell lines by multiple-tissue RNA expression array analysis, Western blot analysis, and immunohistochemistry. ALDP-encoding mRNA is mo...

Journal: :The Canadian journal of neurological sciences. Le journal canadien des sciences neurologiques 2005
Annie Dionne Denis Brunet Alexander McCampbell Nicolas Dupré

BACKGROUND X-linked adrenoleukodystrophy is a peroxisomial disorder caused by mutations in the ABCD1 gene. Adrenomyeloneuropathy is the second most frequent phenotype (25-46%) of this disease and classically presents in adulthood with spastic paraparesis. Female heterozygotes can be symptomatic, but they are frequently misdiagnosed as having multiple sclerosis. CASE REPORT We report a novel m...

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