نتایج جستجو برای: aspartoacylase deficiency

تعداد نتایج: 137211  

2000
M. Quast J. Wei E. L. Ezell P. L. Rady G. A. Campbell K. Matalon J. Ceci S. K. Tyring M. Nehls S. Szucs R. Matalon

Introduction Canavan disease (CD) is an autosomal recessive leukodystrophy associated with spongy degeneration of the white matter of the brain, leading to mental retardation, megalencephaly and early death {I). Brain histology in CD shows characteristic spongy degeneration of the white matter and astrocytic swelling, while neurons are spared. Aspartoacylase (ASPA) deficiency is the basic defec...

Journal: :Journal of the neurological sciences 2016
Rebecca B Roscoe Christina Elliott Apostolos Zarros George S Baillie

Canavan disease (CD) is a rare leukodystrophy characterized by diffuse spongiform white matter degeneration, dysmyelination and intramyelinic oedema with consequent impairment of psychomotor development and early death. The molecular cause of CD has been identified as being mutations of the gene encoding the enzyme aspartoacylase (ASPA) leading to its functional deficiency. The physiological ro...

Journal: :Molecular Genetics and Metabolism 2014

2016
Ai Nishitani Miyuu Tanaka Saki Shimizu Naofumi Kunisawa Mayuko Yokoe Yusaku Yoshida Toshiro Suzuki Tetsushi Sakuma Takashi Yamamoto Mitsuru Kuwamura Shigeo Takenaka Yukihiro Ohno Takashi Kuramoto

Essential tremor (ET) is a common movement disorder with a poorly understood etiology. The TRM/Kyo mutant rat, showing spontaneous tremor, is an animal model of ET. Recently, we demonstrated that tremors in these rats emerge when two mutant loci, a missense mutation in the hyperpolarization-activated cyclic nucleotide-gated potassium channel 1 (Hcn1) and the tremor (tm) deletion, are present si...

2014
Georg von Jonquieres Kristina E. Froud Claudia B. Klugmann Ann C. Y. Wong Gary D. Housley Matthias Klugmann

Canavan Disease (CD) is a leukodystrophy caused by homozygous null mutations in the gene encoding aspartoacylase (ASPA). ASPA-deficiency is characterized by severe psychomotor retardation, and excessive levels of the ASPA substrate N-acetylaspartate (NAA). ASPA is an oligodendrocyte marker and it is believed that CD has a central etiology. However, ASPA is also expressed by Schwann cells and AS...

Journal: :Journal of Cerebral Blood Flow & Metabolism 2012

Journal: :Journal of neurological disorders 2014
Seemin Seher Ahmed Guangping Gao

The blood brain barrier (BBB) refers to the complex anatomical barrier in the brain composed of endothelial cells, astroglia, pericytes, perivascular macrophages and basal lamina. Its selectivity controls the entry of substances into the Central Nervous System (CNS) [1]. BBB disruption affects neurodegeneration [2] and in some cases can be harnessed to deliver intravenous therapeutics to the CN...

نمودار تعداد نتایج جستجو در هر سال

با کلیک روی نمودار نتایج را به سال انتشار فیلتر کنید