نتایج جستجو برای: canavan disease

تعداد نتایج: 1490117  

Journal: :Obstetrics and gynecology 2009

Certain autosomal recessive disease conditions are more prevalent in individuals of Eastern European Jewish (Ashkenazi) descent. Previously, the American College of Obstetricians and Gynecologists recommended that individuals of Eastern European Jewish ancestry be offered carrier screening for Tay-Sachs disease, Canavan disease, and cystic fibrosis as part of routine obstetric care. Based on th...

Journal: :iranian journal of child neurology 0
mahmoodreza ashrafi 1. pediatric neurology division, growth and development research center, children’s medical center, pediatric center of excellence, tehran university of medical science, tehran, iran alireza tavasoli 1. pediatric neurology division, growth and development research center, children’s medical center, pediatric center of excellence, tehran university of medical science, tehran, iran pegah katibeh 1. pediatric neurology division, growth and development research center, children’s medical center, pediatric center of excellence, tehran university of medical science, tehran, iran omid aryani 2. department of medical genetic, national institute for genetic engineering and biotechnology, tehran, iran mohammad vafaee-shahi 1. pediatric neurology division, growth and development research center, children’s medical center, pediatric center of excellence, tehran university of medical science, tehran, iran

how to cite this article: ashrafi mr, tavasoli ar, katibeh p, aryani o, vafaee-shahi m. a novel mutation in aspartoacylase gene; canavan disease. iran j child neurol. autumn 2015; 9(4): 54-57. abstract objective canavan disease (cd) is a type of vacuolating leukodystrophy with autosomal recessive inheritance. aspartoacylase deficiency results in decrease of myelin biosynthesis, dysmyelination a...

Journal: :Journal of the Neurological Sciences 2016

1981
Ronald Brown Philip J. Higgins

The Seifert-van Kampen Theorem involves the category Top∗ of spaces with base-point, the category Group of groups and the fundamental group functor π1 : Top∗ → Group; the theorem asserts that the functor π1 preserves certain special colimits. The generalisation of this theorem to all dimensions thus requires answers to three immediate questions, namely, what are the appropriate generalisations ...

Journal: :Human gene therapy 2002
Christopher Janson Scott McPhee Larissa Bilaniuk John Haselgrove Mark Testaiuti Andrew Freese Dah-Jyuu Wang David Shera Peter Hurh Joan Rupin Elizabeth Saslow Olga Goldfarb Michael Goldberg Ghassem Larijani William Sharrar Larisa Liouterman Angelique Camp Edwin Kolodny Jude Samulski Paola Leone

This clinical protocol describes virus-based gene transfer for Canavan disease, a childhood leukodystrophy. Canavan disease, also known as Van Bogaert-Bertrand disease, is a monogeneic, autosomal recessive disease in which the gene coding for the enzyme aspartoacylase (ASPA) is defective. The lack of functional enzyme leads to an increase in the central nervous system of the substrate molecule,...

2014
Marina R. Carpinelli Anne K. Voss Michael G. Manning Ashwyn A. Perera Anne A. Cooray Benjamin T. Kile Rachel A. Burt

Canavan disease is a leukodystrophy caused by mutations in the ASPA gene. This gene encodes the enzyme that converts N-acetylaspartate into acetate and aspartic acid. In Canavan disease, spongiform encephalopathy of the brain causes progressive mental retardation, motor deficit and death. We have isolated a mouse with a novel ethylnitrosourea-induced mutation in Aspa. This mutant, named deaf14,...

Journal: :Journal of the neurological sciences 2016
Rebecca B Roscoe Christina Elliott Apostolos Zarros George S Baillie

Canavan disease (CD) is a rare leukodystrophy characterized by diffuse spongiform white matter degeneration, dysmyelination and intramyelinic oedema with consequent impairment of psychomotor development and early death. The molecular cause of CD has been identified as being mutations of the gene encoding the enzyme aspartoacylase (ASPA) leading to its functional deficiency. The physiological ro...

Journal: :Advances in experimental medicine and biology 2006
Reuben Matalon Kimberlee Michals-Matalon Sankar Surendran Stephen K Tyring

Canavan disease (CD) is an autosomal recessive disorder, characterized by spongy degeneration of the brain. Patients with CD have aspartoacylase (ASPA) deficiency, which results accumulation of N-acetylaspartic acid (NAA) in the brain and elevated excretion of urinary NAA. Clinically, patients with CD have macrocephaly, mental retardation and hypotonia. A knockout mouse for CD which was enginee...

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