نتایج جستجو برای: tuberous sclerosis complex tsc

تعداد نتایج: 845362  

2017
John C. Kingswood Guillaume B. d’Augères Elena Belousova José C. Ferreira Tom Carter Ramon Castellana Vincent Cottin Paolo Curatolo Maria Dahlin Petrus J. de Vries Martha Feucht Carla Fladrowski Gabriella Gislimberti Christoph Hertzberg Sergiusz Jozwiak John A. Lawson Alfons Macaya Rima Nabbout Finbar O’Callaghan Mirjana P. Benedik Jiong Qin Ruben Marques Valentin Sander Matthias Sauter Yukitoshi Takahashi Renaud Touraine Sotiris Youroukos Bernard Zonnenberg Anna C. Jansen

BACKGROUND Tuberous sclerosis complex (TSC) is a rare autosomal dominant genetic disorder. Many gaps remain in the understanding of TSC because of the complexity in clinical presentation. The TuberOus SClerosis registry to increase disease Awareness (TOSCA) is an international disease registry designed to address knowledge gaps in the natural history and management of TSC. Here, we present the ...

Journal: :Archivos argentinos de pediatria 2017
Gabriela Caicedo-Herrera Estephania Candelo Harry Pachajoa

Tuberous sclerosis complex (TSC) is a neurocutaneous autosomal dominant disorder that results from mutations within either the TSC1 gene or the TSC2 gene. Diagnosis is based on well-established clinical criteria or genetic criteria. Clinical features are highly variable and could be developing over the life. We present a case of TSC with a molecular test that identified a novel variant in TSC2 ...

2017
Bibek S. Pannu Dinesh R. Apala Aditya Kotecha Jennifer M. Boland Vivek N. Iyer

Multifocal micronodular pneumocyte hyperplasia (MMPH) is rare entity seen mostly in patients with the tuberous sclerosis complex (TSC). We present the case of a 50 year old woman with TSC (confirmed TSC2 mutation) found to have multiple ground glass opacities with an upper lobe predominance on a screening chest CT. No abnormalities were detected in other viscera. A thoracoscopic lung biopsy obt...

Journal: :Arquivos de neuro-psiquiatria 2010
Nidia Karen Castillón-Benavides Citlaltepetl Salinas-Lara Francisco Ponce-Guerrero Pablo León Noemí Gelista Martha Lilia Tena-Suck

Unidad Académica de Medicina de la Universidad Autónoma de Nayarit, México; Departamento de Neuropatología. Instituto Nacional de Neurología y Neurocirugía Manuel Velasco Suárez, México; Servicio de Neurocirugía, Instituto Nacional de Neurología y Neurocirugía Manuel Velasco Suárez, México; Servicio de Neuropsiquiatría, Instituto Nacional de Neurología y Neurocirugía Manuel Velasco Suárez, Méxi...

Journal: :Canadian Journal of Neurological Sciences 2022

Background: Tuberous Sclerosis Complex (TSC) is a genetic disease that affects multiple body systems with the neurological manifestations causing greatest burden. The objective of this study was to understand scope TSC care delivery across Canada. Methods: A survey developed after literature review and discussion amongst two Paediatric Epileptologists one Nurse Practitioner expertise in TSC. Ca...

Journal: :Clinical genetics 2014
S Boronat E A Shaaya C M Doherty P Caruso E A Thiele

Tuberous sclerosis complex (TSC) is caused by a mutation in the TSC1 or TSC2 genes. However, 15% of patients have no mutation identified. Tubers and subependymal nodules (SENs) are the typical brain lesions in TSC and are present in 90-95% of patients. The objective of this study is to characterize the specific genotype-phenotype of patients without these lesions. We analyzed the features of 11...

Journal: :European journal of paediatric neurology : EJPN : official journal of the European Paediatric Neurology Society 2010
Roberta Bombardieri Mariangela Pinci Romina Moavero Caterina Cerminara Paolo Curatolo

Epilepsy associated with tuberous sclerosis complex (TSC) is characterized by early onset and intractable seizures in the majority of children. There is a solid evidence of clinical efficacy of vigabatrin in interrupting infantile spasms associated with TSC. Due to an early diagnosis we were able to start vigabatrin at the very early onset of seizures in 10 children, who subsequently underwent ...

2017
Peter J Klover Rajesh L Thangapazham Jiro Kato Ji-An Wang Stasia A Anderson Victoria Hoffmann Wendy K Steagall Shaowei Li Elizabeth McCart Neera Nathan Joshua D Bernstock Matthew D Wilkerson Clifton L Dalgard Joel Moss Thomas N Darling

Increased mTORC1 signaling from TSC1/TSC2 inactivation is found in cancer and causes tuberous sclerosis complex (TSC). The role of mesenchymal-derived cells in TSC tumorigenesis was investigated through disruption of Tsc2 in craniofacial and limb bud mesenchymal progenitors. Tsc2cKOPrrx1-cre mice had shortened lifespans and extensive hamartomas containing abnormal tortuous, dilated vessels prom...

Journal: :Annals of the New York Academy of Sciences 2006
Peter B Crino Katherine L Nathanson Elizabeth Petri Henske

Tuberous sclerosis complex (TSC) is an autosomal dominant disorder that results from mutations in the TSC1 or TSC2 genes and is associated with hamartoma formation in multiple organ systems. The neurological manifestations of TSC are particularly challenging and include infantile spasms, intractable epilepsy, cognitive disabilities, and autism. Progress over the past 15 years has demonstrated t...

Journal: :The Journal of Cell Biology 2004
Elena Goncharova Dmitry Goncharov Daniel Noonan Vera P. Krymskaya

Tuberous sclerosis complex (TSC) 1 and TSC2 are thought to be involved in protein translational regulation and cell growth, and loss of their function is a cause of TSC and lymphangioleiomyomatosis (LAM). However, TSC1 also activates Rho and regulates cell adhesion. We found that TSC2 modulates actin dynamics and cell adhesion and the TSC1-binding domain (TSC2-HBD) is essential for this functio...

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