نتایج جستجو برای: gene defect

تعداد نتایج: 1219432  

2016
Hannadi Alamri Fuad Al Mutairi Johara Alothman Ali Alothaim Majid Alfadhel Ahmed Alfares

Clinicians should consider the EIF2B1 gene defect in any patient with diffuse white matter disease on an MRI of the brain and DKA.

Journal: :Human molecular genetics 1998
P Björses J Aaltonen N Horelli-Kuitunen M L Yaspo L Peltonen

The molecular background of human autoimmunity is poorly understood. Although many autoimmune diseases have a genetic basis, the actual disease appearance results from a complex interplay between genes and environment and thus these diseases represent typical multifactorial diseases. Even with molecular tools provided by the Human Genome Project, it still remains a challenge to identify the pre...

Journal: :Investigative ophthalmology & visual science 1988
G Inana Y Hotta C Zintz K Takki R G Weleber N G Kennaway K Nakayasu A Nakajima T Shiono

A generalized deficiency in the mitochondrial enzyme, ornithine aminotransferase (OAT: EC 2.6.1.13), is the hallmark of gyrate atrophy (GA), a hereditary degenerative disease of the choroid and retina of the eye that leads to blindness. A human OAT cDNA, previously constructed and characterized in our laboratory, and anti-human OAT antibody were used as probes to examine the OAT gene, mRNA and ...

Journal: :Archives of neurology 2005
Miguel A Martín Alberto Blázquez Luis G Gutierrez-Solana Daniel Fernández-Moreira Paz Briones Antoni L Andreu Rafael Garesse Yolanda Campos Joaquín Arenas

BACKGROUND Mutations in the nuclear-encoded subunits of complex I of the mitochondrial respiratory chain are a recognized cause of Leigh syndrome (LS). Recently, 6 mutations in the NDUFS1 gene were identified in 3 families. OBJECTIVE To describe a Spanish family with LS, complex I deficiency in muscle, and a novel mutation in the NDUFS1 gene. DESIGN Using molecular genetic approaches, we id...

Journal: :The Journal of clinical endocrinology and metabolism 1997
Z Hochberg A Van Lieburg L Even B Brenner N Lanir B A Van Oost N V Knoers

Vasopressin V2 receptors, expressed from an x-chromosomal gene, are involved in antidiuresis, but also in release of coagulation factor VIII and von Willebrand factor (vWF). The present study describes autosomal recessive nephrogenic diabetes insipidus (NDI) in a large cluster of patients in Israel's Lower-Galilee. Evidence for an intact V2 receptor was concluded by their normal increase in fac...

2015
Ke Tian Min Qi Limin Wang Zhifu Li Jianzhong Xu Yi Li Guanlei Liu Bing Wang Johnny Huard Guangheng Li

BACKGROUND The major disadvantage of using a stem cell-based bone morphogenetic protein-4 (BMP4) gene therapy for skull defect is the overgrowth of generated bone tissue in situ. In the present study, to overcome bony overgrowth of stem cell based-gene therapy, a new strategy of two-stage bone tissue engineering by an adeno-associated virus containing BMP4 gene (AAV-BMP4) gene therapy was used....

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