نتایج جستجو برای: phenylketonurias

تعداد نتایج: 791  

2004
C. J. Glueck M. T. Schultz S. McNeely

We describe an electroimmunodiffusion technique for measuring /3-lipoprotein in cord blood spotted on filter paper. A series of cord-blood samples, taken from 916 consecutive live-birth infants, was spotted directly onto filter paper and assayed for /3-lipoprotein. Eleven had abovenormal /3-lipoprotein. Of these 11, seven were tested two to six months later, along with their parents, for total ...

2015
Mojca Zerjav Tansek Urh Groselj Natalija Angelkova Dana Anton Ivo Baric Maja Djordjevic Lindita Grimci Maria Ivanova Adil Kadam Vjosa Kotori Hajrija Maksic Oana Marginean Otilia Margineanu Olivera Miljanovic Florentina Moldovanu Mariana Muresan Michaela Nanu Mira Samardzic Vladimir Sarnavka Aleksei Savov Maja Stojiljkovic Biljana Suzic Radka Tincheva Husref Tahirovic Alma Toromanovic Natalia Usurelu Tadej Battelino

BACKGROUND We aimed to assess the current state of PKU screening and management in the region of southeastern Europe. METHODS A survey was performed involving all identified professionals responsible for the PKU management in the 11 countries from South-Eastern region of Europe (Albania, Bulgaria, Bosnia and Herzegovina, Croatia, Kosovo, Macedonia, Moldova, Montenegro, Romania, Serbia, Sloven...

Journal: :Proceedings of the National Academy of Sciences of the United States of America 1974
A E Andersen V Rowe G Guroff

The biochemical features of phenylketonuria have been reproduced in developing rat pups by administering to them a combination of p-chloro-DL-phenylalanine plus L-phenylalanine for the first 21 days after birth. During the treatment period, the experimental animals show delayed eye opening and decreased brain weight compared with controls given saline. Neuropathological examination of developin...

Journal: :The Journal of pediatrics 2014
Rianne Jahja Stephan C J Huijbregts Leo M J de Sonneville Jaap J van der Meere Francjan J van Spronsen

OBJECTIVES To compare the neurocognitive outcomes of patients with phenylketonuria (PKU) to determine whether decreasing phenylalanine (Phe) levels to <240 is preferable to the use of 360 μmol/L as an upper-target Phe level. An additional aim was to establish the influence of biochemical indices other than Phe on neurocognitive outcomes. STUDY DESIGN Patients with PKU (n = 63; mean age 10.8 ±...

2013
Astrid Fidika Christel Salewski Lutz Goldbeck

BACKGROUND Parents of children with chronic conditions are known to be at risk of impairment in their quality of life (QoL). Studies considering other chronic conditions proposed diverse factors to have an impact on the parent's QoL. So far, there has been little research on parents who have a child with phenylketonuria (PKU). This study was designed to evaluate the parental quality of life (PQ...

Journal: :Molecular genetics and metabolism 2010
Darren Janzen Mina Nguyen

Individuals with early-treated phenylketonuria (ETPKU) most often present with impairment in executive function (EF) and average intelligence compared to the general population. The topic of this review, which is less often discussed, is non-EF impairments that may be associated with ETPKU. Studies that have included assessment of non-EF cognitive functions such as information processing speed,...

2007
Supriya Srinivasa Gowda David McDonald

Phenylketonuria (PKU) is an inborn error in the metabolism of the amino acid phenylalanine (Phe) due to the deficiency of an enzyme phenylalanine hydroxylase (PAH). Current therapy consists of a Phe – restricted diet for life to ensure the healthiest development. It is particularly important for PKU women in the reproductive age group to comply with the diet, since elevated maternal blood Phe l...

Journal: :Science advances 2015
Shira Shaham-Niv Lihi Adler-Abramovich Lee Schnaider Ehud Gazit

The accumulation of amyloid fibrils is the hallmark of several major human diseases. Although the formation of these supramolecular entities has previously been associated with proteins and peptides, it was later demonstrated that even phenylalanine, a single amino acid, can form fibrils that have amyloid-like biophysical, biochemical, and cytotoxic properties. Moreover, the generation of antib...

2014
Virender Singh Ratan Kumar Rai Ashish Arora Neeraj Sinha Ashwani Kumar Thakur

Self-assembly of phenylalanine is linked to amyloid formation toxicity in phenylketonuria disease. We are demonstrating that L-phenylalanine self-assembles to amyloid fibrils at varying experimental conditions and transforms to a gel state at saturated concentration. Biophysical methods including nuclear magnetic resonance, resistance by alpha-phenylglycine to fibril formation and preference of...

Journal: :Journal of medical genetics 1989
L A Tyfield A L Meredith M J Osborn P S Harper

Using the full length cDNA probe, the RFLP haplotype patterns at the phenylalanine hydroxylase locus have been studied in the extensive and highly consanguineous Welsh Gypsy population. The pattern associated with the mutant PKU allele is identical to haplotype 4 in the northern European population. Two children with classical PKU are homozygous for this haplotype. We have tracked the mutant al...

نمودار تعداد نتایج جستجو در هر سال

با کلیک روی نمودار نتایج را به سال انتشار فیلتر کنید