نتایج جستجو برای: friedreich ataxia frda

تعداد نتایج: 17926  

2014
Barbara Carletti Fiorella Piemonte

A prominent feature of Friedreich's ataxia (FRDA) is the neurodegeneration of the central and peripheral nervous systems, but little information is available about the mechanisms leading to neuronal damage in this pathology. Currently, no treatments delay, prevent, or reverse the inexorable decline that occurs in this condition. Evidence of oxidative damage has been demonstrated in Friedreich's...

Journal: :Human molecular genetics 1997
V Campuzano L Montermini Y Lutz L Cova C Hindelang S Jiralerspong Y Trottier S J Kish B Faucheux P Trouillas F J Authier A Dürr J L Mandel A Vescovi M Pandolfo M Koenig

Friedreich ataxia is a progressive neurodegenerative disorder caused by loss of function mutations in the frataxin gene. In order to unravel frataxin function we developed monoclonal antibodies raised against different regions of the protein. These antibodies detect a processed 18 kDa protein in various human and mouse tissues and cell lines that is severely reduced in Friedreich ataxia patient...

Journal: :Human molecular genetics 2008
Stéphane Schmucker Manuela Argentini Nadège Carelle-Calmels Alain Martelli Hélène Puccio

Deficiency in the nuclear-encoded mitochondrial protein frataxin causes Friedreich ataxia (FRDA), a progressive neurodegenerative disorder associating spinocerebellar ataxia and cardiomyopathy. Although the exact function of frataxin is still a matter of debate, it is widely accepted that frataxin is a mitochondrial iron chaperone involved in iron-sulfur cluster and heme biosynthesis. Frataxin ...

2018
Marta Seco-Cervera Dayme González-Rodríguez José Santiago Ibáñez-Cabellos Lorena Peiró-Chova Federico V Pallardó José Luis García-Giménez

Friedreich's ataxia (FRDA; OMIM 229300), an autosomal recessive neurodegenerative mitochondrial disease, is the most prevalent hereditary ataxia. In addition, FRDA patients have shown additional non-neurological features such as scoliosis, diabetes, and cardiac complications. Hypertrophic cardiomyopathy, which is found in two thirds of patients at the time of diagnosis, is the primary cause of ...

2014
Sahar Al-Mahdawi Sara Anjomani Virmouni Mark A. Pook

DNA methylation primarily occurs within human cells as a 5-methylcytosine (5mC) modification of the cytosine bases in CpG dinucleotides. 5mC has proven to be an important epigenetic mark that is involved in the control of gene transcription for processes such as development and differentiation. However, recent studies have identified an alternative modification, 5-hydroxymethylcytosine (5hmC), ...

Journal: :genetics in the 3rd millennium 0
مسعود هوشمند massoud houshmand assist prof of molecular genetic, national institute for genetic engineering and biotechnology, tehran, iran شهریار نفیسی shahriar nafisi محمد حیدری mohammad heydari سپیده صفایی sepideh safaie امید آریانی omid aryani اکبر سلطان زاده akbar soltanzadeh مهدی شفا

the hereditary ataxias are a group of genetic disorders characterized by slowly progressive incoordination of gait and often associated with poor coordination of hands, speech, and eye movements. frequently, atrophy of the cerebellum occurs. the hereditary ataxias are categorized by mode of inheritance and causative gene or chromosomal locus. genetic forms of ataxia must be distinguished from t...

Journal: :Movement Disorders Clinical Practice 2014

2010
Kuanyu Li Anamika Singh Daniel R. Crooks Xiaoman Dai Zhuangzhuang Cong Liang Pan Dung Ha Tracey A. Rouault

BACKGROUND Friedreich ataxia is an autosomal recessive neurodegenerative disease caused by reduced expression levels of the frataxin gene (FXN) due to expansion of triplet nucleotide GAA repeats in the first intron of FXN. Augmentation of frataxin expression levels in affected Friedreich ataxia patient tissues might substantially slow disease progression. METHODOLOGY/PRINCIPAL FINDINGS We uti...

Journal: :Journal of Medical Genetics 2000

نمودار تعداد نتایج جستجو در هر سال

با کلیک روی نمودار نتایج را به سال انتشار فیلتر کنید