نتایج جستجو برای: duchenne

تعداد نتایج: 8037  

2016
Luca Bello Akanchha Kesari Heather A. Gordish-Dressman Avital Cnaan Lauren P Morgenroth Jaya Punetha Tina Duong Erik Henricson Elena Pegoraro Craig M. McDonald Eric P. Hoffman Heather Gordish-Dressman Lauren P. Morgenroth Erik K. Henricson

Genetic modifiers of ambulation in the CINRG duchenne natural history study.

Journal: :Proceedings of the Royal Society of Medicine 1973

Journal: :Revista Eletrônica Acervo Saúde 2023

Objetivo: Analisar as características da Distrofia Muscular de Duchenne (DMD). Revisão bibliográfica: A DMD é a distrofia muscular infantil mais comum em todo o mundo, sendo uma doença recessiva ligada ao X, causada por mutações no gene que codifica distrofina, afetando 1 3.500 5.000 meninos. distrofina grande proteína do citoesqueleto facilita interações entre citoesqueleto, membrana celular e...

2013
Zoe Davidson Michael Cheung

Duchenne muscular dystrophy (DMD) affects approximately 1 in 3,500 live male births [1]. It is caused by a large variety of mutations in the dystrophin gene. Because of these mutations, the body can no longer make dystrophin which is a protein important for stabilisation of the muscle cell during a contraction. Without dystrophin, muscle cells are damaged and slowly replaced by fat and scar tis...

Journal: :Brain : a journal of neurology 2011
Karen Anthony Sebahattin Cirak Silvia Torelli Giorgio Tasca Lucy Feng Virginia Arechavala-Gomeza Annarita Armaroli Michela Guglieri Chiara S Straathof Jan J Verschuuren Annemieke Aartsma-Rus Paula Helderman-van den Enden Katherine Bushby Volker Straub Caroline Sewry Alessandra Ferlini Enzo Ricci Jennifer E Morgan Francesco Muntoni

Duchenne muscular dystrophy is caused by mutations in the DMD gene that disrupt the open reading frame and prevent the full translation of its protein product, dystrophin. Restoration of the open reading frame and dystrophin production can be achieved by exon skipping using antisense oligonucleotides targeted to splicing elements. This approach aims to transform the Duchenne muscular dystrophy ...

Journal: :American journal of physical medicine & rehabilitation 2011
John Robert Bach Anthony Decicco

Bach JR, DeCicco A: Forty-eight years with Duchenne muscular dystrophy. Am J Phys Med Rehabil 2011;90:868Y870.

Journal: :Neuromuscular disorders : NMD 2002
E A C Beenakker J de Vries J M Fock M van Tol O F Brouwer N M Maurits J H van der Hoeven

Duchenne muscular dystrophy is clinically characterised by progressive muscle weakness and a gradual increase in the size of some affected muscles, especially calf muscles. The extent of calf enlargement is usually determined by subjective visual assessment. The purpose of this study was to determine the extent of calf muscle enlargement in Duchenne muscular dystrophy (DMD) patients compared wi...

Journal: :Journal of medical genetics 1992
A Miciak A Keen D Jadayel S Bundey

We have investigated an extended pedigree with three cousins affected by Duchenne muscular dystrophy with apparent transmission through the male line. However, molecular studies have shown that one boy has a de novo duplication, another has a deletion, and the molecular mutation has yet to be defined in the third boy. All three X chromosomes in the affected boys appear to have a different origi...

Journal: :Seminars in respiratory and critical care medicine 2002
Anita K Simonds

Pulmonary complications including chest infections, atelectasis, pulmonary hypoplasia and ventilatory failure are the leading cause of death in the muscular dystrophies and atrophies. Ventilatory insufficiency is virtually inevitable in Duchenne muscular dystrophy and type 1 spinal muscular atrophy (SMA), but more variable in limb-girdle, congenital, and facioscapulohumeral muscular dystrophy. ...

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