نتایج جستجو برای: dystrophin related protein 2 gene drp2

تعداد نتایج: 4828568  

Journal: :BMC Medicine 2007
Richard T Hinkle Frank R Lefever Elizabeth T Dolan Deborah L Reichart Jefferey A Dietrich Kathryn E Gropp Robert I Thacker Jeffrey P Demuth Paula J Stevens Xiaoyan A Qu Alex R Varbanov Feng Wang Robert J Isfort

BACKGROUND Duchenne muscular dystrophy results from mutation of the dystrophin gene, causing skeletal and cardiac muscle loss of function. The mdx mouse model of Duchenne muscular dystrophy is widely utilized to evaluate the potential of therapeutic regimens to modulate the loss of skeletal muscle function associated with dystrophin mutation. Importantly, progressive loss of diaphragm function ...

Journal: :Human molecular genetics 2013
Nikolai Klymiuk Andreas Blutke Alexander Graf Sabine Krause Katinka Burkhardt Annegret Wuensch Stefan Krebs Barbara Kessler Valeri Zakhartchenko Mayuko Kurome Elisabeth Kemter Hiroshi Nagashima Benedikt Schoser Nadja Herbach Helmut Blum Rüdiger Wanke Annemieke Aartsma-Rus Christian Thirion Hanns Lochmüller Maggie C Walter Eckhard Wolf

Duchenne muscular dystrophy (DMD) is caused by mutations in the X-linked dystrophin (DMD) gene. The absence of dystrophin protein leads to progressive muscle weakness and wasting, disability and death. To establish a tailored large animal model of DMD, we deleted DMD exon 52 in male pig cells by gene targeting and generated offspring by nuclear transfer. DMD pigs exhibit absence of dystrophin i...

Journal: :The Journal of clinical investigation 1993
K Matsumura F M Tomé V Ionasescu J M Ervasti R D Anderson N B Romero D Simon D Récan J C Kaplan M Fardeau

Dystrophin, the protein product of the Duchenne muscular dystrophy (DMD) gene, is a cytoskeletal protein tightly associated with a large oligomeric complex of sarcolemmal glycoproteins including dystroglycan, which provides a linkage to the extracellular matrix component, laminin. In DMD, the absence of dystrophin leads to a drastic reduction in all of the dystrophin-associated proteins, causin...

Journal: :Proceedings of the National Academy of Sciences of the United States of America 1994
J M Tinsley D J Blake R A Zuellig K E Davies

Duchenne muscular dystrophy is a severe X chromosome-linked, muscle-wasting disease caused by lack of the protein dystrophin. The exact function of dystrophin remains to be determined. However, analysis of its interaction with a large oligomeric protein complex at the sarcolemma and the identification of a structurally related protein, utrophin, is leading to the characterization of candidate g...

Journal: :Journal of cell science 1994
D J Law D L Allen J G Tidball

Duchenne muscular dystrophy (DMD) and the myopathy seen in the mdx mouse both result from absence of the protein dystrophin. Structural similarities between dystrophin and other cytoskeletal proteins, its enrichment at myotendinous junctions, and its indirect association with laminin mediated by a transmembrane glycoprotein complex suggest that one of dystrophin's functions in normal muscle is ...

2015
Hongmei Lisa Li Naoko Fujimoto Noriko Sasakawa Saya Shirai Tokiko Ohkame Tetsushi Sakuma Michihiro Tanaka Naoki Amano Akira Watanabe Hidetoshi Sakurai Takashi Yamamoto Shinya Yamanaka Akitsu Hotta

Duchenne muscular dystrophy (DMD) is a severe muscle-degenerative disease caused by a mutation in the dystrophin gene. Genetic correction of patient-derived induced pluripotent stem cells (iPSCs) by TALENs or CRISPR-Cas9 holds promise for DMD gene therapy; however, the safety of such nuclease treatment must be determined. Using a unique k-mer database, we systematically identified a unique targ...

2011
Joachim Berger Silke Berger Arie S Jacoby Steve D Wilton Peter D Currie

Duchenne muscular dystophy (DMD) is a severe muscle wasting disease caused by mutations in the dystrophin gene. By utilizing antisense oligonucleotides, splicing of the dystrophin transcript can be altered so that exons harbouring a mutation are excluded from the mature mRNA. Although this approach has been shown to be effective to restore partially functional dystrophin protein, the level of d...

Journal: :The Journal of Cell Biology 1991
K Ohlendieck K P Campbell

Dystrophin, the protein product of the human Duchenne muscular dystrophy gene, exists in skeletal muscle as a large oligomeric complex that contains four glycoproteins of 156, 50, 43, and 35 kD and a protein of 59 kD. Here, we investigated the relative abundance of each of the components of the dystrophin-glycoprotein complex in skeletal muscle from normal and mdx mice, which are missing dystro...

Journal: :iranian journal of child neurology 0
mohammad barzegar 1. pediatric health research center, tabriz university of medical sciences, tabriz, iran. 2. division of pediatric neurology, tabriz children’s hospital, tabriz university of medical sciences, tabriz, iran parinaz habibi 1. pediatric health research center, tabriz university of medical sciences, tabriz, iran. mortaza mortaza bonyady 3. center of excellence for biodiversity, department of molecular medical genetics, faculty of natural sciences university of tabriz, tabriz, iran vahideh topchizadeh 4. physical medicine & rehabilitation research center, tabriz university of medical sciences, tabriz, iran shadi shiva* 1. pediatric health research center, tabriz university of medical sciences, tabriz, iran. 2. division of pediatric neurology, tabriz children’s hospital, tabriz university of medical sciences, tabriz, iran

how to cite this article: barzegar m, habibi p, bonyady m, topchizadeh v, shiva sh. exon deletion pattern in duchene muscular dystrophy in north west of iran. iran j child neurol. 2015 winter; 9(1): 42-48. abstract objective duchene and becker muscular dystrophy (dmd/ bmd) are x-linked disorders that both are the result of heterogeneous mutations in the dystrophin gene. the frequency and distri...

2006
F. Montanaro M. Lindenbaum

F. Montanaro, S. Carbonetto, K.P. Campbell, and M. Lindenbaum Department of Biology, McGill University (F.M., S.C.), Centre for Research in Neuroscience, McGill University, and Montreal General Hospital Research Institute (F.M., S.C., M.L.), Montreal, Canada; and Howard Hughes Medical Institute and Department of Physiology and Biophysics, University of Iowa College of Medicine, Iowa City, Iowa ...

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